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Learning More About Myasthenia Gravis
Myasthenia gravis causes a breakdown in the normal communication between nerves and muscles. This causes weakness and fatigued muscles. The purpose of this study is to help researchers learn more about myasthenia gravis. We will be collecting data and storing blood samples for future research. This is not a treatment study.
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Taking a Look at Stigma and Discrimination Associated with Chronic Tic Disorders
The purpose of this study is to create a new way to measure how stigma and discrimination effects people with chronic tic disorders. The Tourette discrimination-stigmatization scale will be tested through interviews with people who have tics. Caregivers, doctors, and advocates will also be interviewed. We want to better understand the challenges that people with chronic tic disorder might face.
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Learning More About Treating Migraine in Children and Young Adults with Rimegepant
The purpose of this study is to learn how well the study drug, Rimegepant, treats migraines in children and young adults. We also want to learn more about the possible side effects of the study drug.
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Testing the Study Drug NRTX-1001 for Drug-Resistant Epilepsy in the Brain
The purpose of this study is to test if the study drug NRTX-1001 cell therapy is safe for people with drug-resistant mesial temporal lobe epilepsy (MTLE). Another goal is to see if it can reduce the number of seizures you have.
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Treating Inclusion Body Myositis with the Study Drug ABC008
Inclusion body myositis (IBM) is an inflammatory autoimmune disorder of skeletal muscle. With IBM harmful immune cells attack muscle causing muscle weakness. The study drug ABC008 has been designed to reduce the number of these harmful immune cells. The purpose of this study is to find out how well the study drug works for treating IBM.
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New Tool to Measure Progression of Parkinson's Disease
Eye movement tasks have long been used as a measure of sensory, motor, and cognitive function. These tasks can possibly be used as a way to measure the progression of diseases like Parkinson's. The purpose of this study is to create a new tool to measure the progression of Parkinson's disease. Having such a tool could lead to better diagnosis and treatment in the future.
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A Study of the Drug Staccato Alprazolam for Patients with Prolonged Seizures
The purpose of this study is to learn more about the study drug Staccato Alprazolam. We want to see how well the study drug works for treating patients with previous episodes of prolonged seizures. We also want to learn more about the safety and side effects that may be caused by the study drug.
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Can Regular Phone Calls with a Care Manager Improve Quality of Life for People with Post-Traumatic Epilepsy
The purpose of this study is to find out if regular phone calls from a care manager can help patients with post-traumatic epilepsy and symptoms of anxiety and/or depression. The care manager will talk about anxiety, depression, seizures and side effects. They will also provide you with brief therapy sessions. We want to know if this approach helps improve emotional quality of life.
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Finding Out How Well Rimegepant Works for Treating Migraines in People Ages 12 to 17
The purpose of this study is to find out how well the study drug, Rimegepant, works for treating migraines in people age 12 to 17. We also want to find out how safe it is in children and young people.
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Neurology Disorders Pain Brain and Memory Children, Infants, Teen Health
Learning More About the Long-Term Use of the Study Drug Staccato Alprazolam for Prolonged Seizures
The purpose of this study is to learn more about the long-term use of the study drug Staccato Alprazolam. We want to see how well the study drug works when used long-term for patients with a history of prolonged seizures. We also want to learn more about the safety and side effects that may be caused by the study drug.
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Collecting Data on Patients with Generalized Myasthenia Gravis
General Myasthenia Gravis is a rare disease that makes it hard for nerves and muscles to work together. This study collects information about people with this disease in a patient registry. The registry helps scientists learn new things that might help others in the future.
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Neurology Disorders Rare Disease Arthritis, Lupus, and Autoimmune Disorders
Study to See How Well the Study Drug EPX-100 Works for Treating Dravet Syndrome
The purpose of this study is to see how well the study drug, EPX-100, works for treating Dravet syndrome. We also want to learn more about possible side effects.
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Can Listening to Specific Tones Help Decrease Stress in Dementia Caregivers
The purpose of this research study is to find out if six sessions of listening to specific tones can reduce some symptoms of stress.
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Healthy Volunteers Mental Health Neurology Disorders Brain and Memory
Learning More About Transthyretin Familial Amyloid Polyneuropathy
Transthyretin familial amyloid polyneuropathy (TTR?FAP) is a rare disorder some people are born with. It affects nerves and organs and can cause numbness in the legs and numbness or pain in the hands. It can also cause stomach, heart, urinary or sexual problems. The purpose of the study is to find out how common TTR-FAP may be. We also want to learn more about the symptoms.
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A study on the effectiveness of the drug SAR442168 in Participants With Primary Progressive Multiple Sclerosis
The purpose of the study is to see if the study drug, SAR442168, works to delay the progression of disability in people with primary progressive multiple sclerosis (PPMS) compared to placebo (a substance that has no effect). PPMS is one type of Multiple Sclerosis, which is a group of disease that over time, affect your brain's ability to control your body.
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Learning More About Treating Childhood Absence Epilepsy and Juvenile Absence Epilepsy with Brivaracetam
The purpose of this study is to see how well the study drug, brivaracetam, treats childhood absence epilepsy or juvenile absence epilepsy. We also want to learn more about any possible side effects it may cause.
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Care Program for Adults with Epilepsy Dealing with Anxiety and/or Depression
The purpose of this study is to find out if emotional quality of life can be improved for those with epilepsy and anxiety and/or depression. We want to see if regular calls or visits with a care manager can help with the anxiety and/or depression symptoms.
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How Myotonic Dystrophy Type 2 Affects the Brain
Myotonic dystrophy affects the muscles and other body systems. The purpose of this study is to look at the impact myotonic dystrophy type 2 has on the brain. We also want to look at brain-based symptoms like problems with thinking, memory or motivation.
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The HEALEY Trial: Learning More About Different Treatments for ALS
The purpose of this study is to learn more about multiple treatments for amyotrophic lateral sclerosis (ALS). We want to find out if different treatments have an effect on ALS. We also want to find out if these treatments are safe to take without causing too many side effects.
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Collecting Data for Parkinson's Disease Research
The purpose of this study is to gather information on people with Parkinson's disease through a patient registry. The registry will collect genetic information from people with Parkinson's, those at risk, and others without the disease. The registry will help improve understanding and care for Parkinson's disease.
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